Sarepta's Elevidys has been approved for a narrow age range of boys with muscular dystrophy — excruciating for boys who are a hair too old.
Courtesy Secrist family With an age cutoff for a new gene therapy, families and doctors scramble to treat kids before their 6th birthday In July, Kristen Secrist (above, center) hopped on a call with her 5-year-old son's doctor, who had urgent news: The first gene therapy had been approved for Duchenne muscular dystrophy. Her son, Hiram, would be a perfect candidate — if, she added, they could get him dosed in time. Read more. By Jason Mast |
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Mike Reddy for STAT Health care CEOs hauled in $4 billion last year as inflation pinched workers, analysis shows The health care industry didn't just provide a safe haven for jittery stock investors in 2022, a year defined by inflation and higher interest rates. It also provided a stable stream of wealth for top executives, who collectively pocketed billions of dollars in what was otherwise a rough patch for the economy. Read more. By Bob Herman, J. Emory Parker, Adam Feuerstein, Lizzy Lawrence, and Mohana Ravindranath Michelle Gable for STAT Why drug shortages are having an outsize impact on ovarian cancer patients While patients with various types of cancer have been impacted by drug shortages, those with ovarian cancer, like Sarah Evans (above), are among the groups most affected — both because the disease is relatively common and because the drugs that are most effective in treating it are the ones now in short supply. Read more. By Annalisa Merelli More great reads from STAT this week |
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