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This father built a gene therapy for his son. Now comes the harder part: saving others’ children, too 

December 9, 2024
Pharmalot Columnist, Senior Writer
When the Lockhard family was thrust into the bewildering world of ultra-rare disease, they found their way to someone they hoped could help, Terry Pirovolakis.
Rachel Woolf for STAT

STAT+ | This father built a gene therapy for his son. Now comes the harder part: saving others' children, too

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Arlene Ibarra for STAT

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