'Literally overnight, it’s gone'

As Sarepta Therapeutics fights for its Duchenne therapy, a group of patients gets left behind.

August 23, 2025 Check out STAT+

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Shahrzad Rasekh for STAT STAT+ | As Sarepta Therapeutics fights for Duchenne therapy, a group of patients gets left behind After deaths and FDA setbacks, Sarepta abandoned LGMD gene therapy, leaving families desperate and patients without long-promised treatments. By Jason Mast Kayana Szymczak for STAT STAT+ | Can a humble, Harley-riding professor and former Trump adviser fend off science cuts? Kelvin Droegemeier is driving a high-stakes push on NIH indirect costs, with billions in funding and U.S. science leadership on the line By Jonathan Wosen Mike Reddy for STAT STAT+ | Health care CEOs harvest billions even as industry lags broader stock market Annual executive compensation review of prominent health care companies found 275 CEOs earning $3.6 billion in 2024. By Bob Herman and J. Emory Parker STAT+ | AI scribe companies promise to help doctors bill more. Who will pay the extra cost? Note-taking scribes are rapidly growing in use among doctors. Experts say AI bots automatically coding for insurance may lead to higher bills for patients. By Brittany Trang STAT+ | Why direct-to-consumer sales are unlikely to significantly lower drug costs Some experts say the move is unlikely to significantly help consumers, but see no harm in it. Others worry it could let the pharma industry off the hook. By Elaine Chen STAT+ | In a new era, glucose sensors straddle the line between medical device and wellness tool Some startups are beginning to sell over-the-counter continuous glucose monitors directly to users alongside their apps. By Katie Palmer Opinion: The trauma of illness can last long after the body has healed Medicine overlooks the psychological toll of medical illness. Healing must involve helping people repair their relationship with their bodies. By Alexandra Kutnick

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